UW researchers co-published findings March 18 that inform a new approach to targeting the huntingtin gene, specifically ...

“It’s tough to watch everybody get sick,” she adds. “You live in constant worry.” ...

A decade ago, UB researchers shed some light on an enduring neuroscience mystery: How exactly does a mutated huntingtin protein (HTT) cause Huntington’s disease? They found that HTT is something like ...

TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. Assault at Mobile McDonald’s leaves man ...

An experimental gene therapy has become the first treatment to successfully slow the progression of Huntington’s disease. While the findings are still preliminary, the approach could be a major ...

In 1993, 25 years after her family launched their foundation, the group of scientists they supported finally identified the ...

If CRISPR stays active too long, it could cut unintended parts of the genome. To reduce this risk, the researchers designed a self-inactivating CRISPR system. This means that CRISPR edits the gene and ...

Approximately 41,000 Americans live with a rare, genetic, degenerative disorder that is described as a combination of ALS, ...

9 min read |New research in a HD mouse model points to a key culprit: a small fragment called HTT1a. Lowering HTT1a levels successfully delayed disease signs in mice that model HD, perhaps shaping the ...