Jagadeesha's brain, the first juvenile Huntington's Disease donation in India, offers hope for vital neurodegenerative ...
A new discovery offers hope for Huntington’s disease. This discovery provides hope that a DNA repair process may help slow or stop disease progression. Research has identified a critical DNA repair ...
Huntington’s disease is a hereditary disorder that causes a progressive decline in thinking, memory, and the control of movements. On average, the symptoms begin when a person is in their early 40s, ...
October was an insight-rich month in Huntington’s disease research: additional clarity around uniQure’s AMT-130, mapping how and where HD changes the brain, early mechanistic studies targeting DNA ...
Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...
LEXINGTON, Mass. and AMSTERDAM, Nov. 03, 2025 (GLOBE NEWSWIRE) -- uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing ...
UniQure, said on Monday the U.S. Food & Drug Administration has deemed clinical data for its gene therapy for Huntington's ...
UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...
Sept. 24 (UPI) --Researchers at University College London reported success in treating Huntington's disease with gene therapy, which is the world's first to prove successful. The gene therapy slowed ...
AMT-130, aimed at treating Huntington’s disease (HD). This article will delve into the recent feedback from the U.S. Food and Drug Administration (FDA), the implications for the therapy's regulatory ...